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Design of a Global Phase 3, Randomized, Double-Blind, Placebo-Controlled Trial of AMX0035 in Progressive Supranuclear Palsy (A35-009 ORION)

Lead Author: Günter Höglinger, MD

Published: Neuro2023

Date: October 19 - 20, 2023

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Analysis of Sodium Phenylbutyrate and Taurursodiol Survival Effect in ALS Using External Controls

Lead Author: Sabrina Paganoni, MD, PhD & Melanie Quintana, PhD

Published: Annals of Clinical and Translational Neurology

Date: October 9, 2023

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An In Vitro Recovery Study of Sodium Phenylbutyrate and Taurursodiol From 3 Types of Dosing Containers and Various Percutaneous Endoscopic Gastrostomy Feeding Tubes

Lead Author: Machelle Manuel, PhD

Published: Northeast ALS Consortium Annual Meeting (NEALS)

Date: October 4 - 6, 2023

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Development of a Composite Diagnostic Biomarker for Amyotrophic Lateral Sclerosis: Experimental Approach and Progress to Date

Lead Author: Jamie Timmons, MD

Published: Northeast ALS Consortium Annual Meeting (NEALS)

Date: October 4 - 6, 2023

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Novel Neuroprotective Strategies in Human Neuron Models of ALS/FTD: Evaluating Antisense Oligonucleotide Therapies, including AMX0114

Lead Author: Sami Barmada, MD, PhD

Published: Northeast ALS Consortium Annual Meeting (NEALS)

Date: October 4 - 6, 2023

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Ongoing and Planned Studies to Further Elucidate the Efficacy, Safety, and Pharmacokinetics of Sodium Phenylbutyrate and Taurursodiol in Amyotrophic Lateral Sclerosis

Lead Author: Jamie Timmons, MD

Published: Northeast ALS Consortium Annual Meeting (NEALS)

Date: October 4 - 6, 2023

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Preliminary Experience With Sodium Phenylbutyrate and Taurursodiol in a United States Expanded Access Program

Lead Author: Machelle Manuel, PhD

Published: Northeast ALS Consortium Annual Meeting (NEALS)

Date: October 4 - 6, 2023

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Real-World Experience and Strategies to Enhance the Palatability of the Combination Sodium Phenylbutyrate and Taurursodiol for the Treatment of Amyotrophic Lateral Sclerosis

Lead Author: Jamie Timmons, MD

Published: Northeast ALS Consortium Annual Meeting (NEALS)

Date: October 4 - 6, 2023

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Update on AMX0114: An Antisense Oligonucleotide Targeting Calpain-2, a Critical Effector of Axonal Degeneration

Lead Author: Jamie Timmons, MD

Published: Northeast ALS Consortium Annual Meeting (NEALS)

Date: October 4 - 6, 2023

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Characterization of the Enrolled Population in the Phase 3 PHOENIX Trial in Amyotrophic Lateral Sclerosis: Preliminary Results

Lead Author: Leonard van den Berg (Presenter)

Published: European Network to Cure ALS (ENCALS)

Date: July 12 - 14, 2023

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